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hero-preparing-for-gene-therapy-trials
November 17, 2017
Preparing for Gene Therapy Trials
hero-breakthroughs-rna-editing
November 8, 2017
Breakthrough Discoveries for DNA & RNA Editing
hero-editing-out-rett-mutations
October 26, 2017
Editing Out Rett Mutations
hero-bridging-the-divide
October 11, 2017
Bridging the Divide
hero-what-about-us
July 12, 2017
What About Us?
hero-precision-medicine
June 19, 2017
Precision Medicine
hero-avexis-announcement-delivering-on-roadmap-to-a-cure
June 8, 2017
AveXis Announcement - Delivering on Roadmap to a Cure
hero-gene-therapy-consortium-reports-on-progress
May 15, 2017
Gene Therapy Consortium Reports on Progress
hero-gene-therapy-primer
May 10, 2017
Gene Therapy Primer
hero-racing-down-the-gene-therapy-highway-to-a-cure
April 25, 2017
Racing Down The Gene Therapy Highway To A Cure
hero-orphan-drug-meaning
March 30, 2017
Orphan Drug Designation: What Does it Mean?
hero-new-insight-into-mecp2-mutation-hotspot
March 27, 2017
New Insight Into MECP2 Mutation Hotspot
hero-roadmap-faq
March 24, 2017
Roadmap to a Cure FAQ
hero-rsrt-awards-7-5-million-to-research-in-2016
March 17, 2017
RSRT Awards $7.5 Million to Research in 2016
hero-key-questions-clinical-trials
February 28, 2017
Key Questions to Ask When Considering Clinical Trials
hero-awaken-activate-mighty-x-chromosome
February 2, 2017
Awaken and Activate the Mighty X Chromosome
hero-of-mice-and-rett-novel-therapeutics-community-support
January 27, 2017
Of Mice and Rett: Novel Therapeutics & Community Support
hero-rare-disease-drug-approval-sparks-controversy
December 14, 2016
Rare Disease Drug Approval Sparks Controversy
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