Skip to main content
Search
Cures
Roadmap to Cures
Where We’ve Been
Roadmap 1.0
Delivery
Viral
Non-Viral
Small RNA
Cargo
Gene Therapy
Base Editing
Prime Editing
MECP2 Reactivation
RNA Editing
RNA Trans-splicing
Tracking
Rett Syndrome Global Registry
Citizen Health
Biomarkers
Biosensors
VIBRANT
Families
Was your child
recently diagnosed?
We’re here for you.
Reach Out Now
Recently Diagnosed
For All Families
About Rett Syndrome
Genetics Primer
Rett Syndrome Global Registry
Rett Clinics & Clinical Trials
Thriving with Rett Guides
Rett Fact Cards
Researchers
Fundraise
Start Your Own
Crowdfunding Page
We’ll get you set up!
Get Started
Get Started Now
Join Us
Events
RettGive Campaigns
Facebook Fundraisers
Donate
About Us
News
Get timely, factual news about Rett syndrome.
Browse News
Articles
Research
Community
Fundraising
Press Releases
Rett in the News
Donate
Join Us
Donate
Join Us
Cures
Roadmap to Cures
Where We’ve Been
Roadmap 1.0
Delivery
Viral
Non-Viral
Small RNA
Cargo
Gene Therapy
Base Editing
Prime Editing
MECP2 Reactivation
RNA Editing
RNA Trans-splicing
Tracking
Rett Syndrome Global Registry
Citizen Health
Biomarkers
Biosensors
VIBRANT
Families
Recently Diagnosed
For All Families
About Rett Syndrome
Genetics Primer
Rett Syndrome Global Registry
Rett Clinics & Clinical Trials
Thriving with Rett Guides
Rett Fact Cards
Researchers
Fundraise
Get Started Now
Join Us
Events
RettGive Campaigns
Facebook Fundraisers
Donate
About Us
News
Articles
Research
Community
Fundraising
Press Releases
Rett in the News
Rett Syndrome Global Registry
RettGive
Search
Taysha
October 2, 2025
Taysha Receives FDA Breakthrough Therapy Designation for TSHA-102
August 12, 2025
Taysha Advances REVEAL Pivotal Trial for Rett Syndrome
April 18, 2025
How Will Cuts to FDA and NIH Impact Gene Therapy Clinical Trials and Rett Syndrome Research?
January 15, 2025
A Review of Gene Therapy Clinical Trials
November 13, 2024
Taysha Releases Financial, Enrollment Update and Community Letter
August 12, 2024
Taysha Rett Program Updates Q2 2024
June 18, 2024
Taysha Announced New Clinical Data from the REVEAL Phase 1/2 Adolescent & Pediatric Trial Evaluating TSHA-102
March 19, 2024
Taysha Rett Program Updates March 2024
February 29, 2024
Taysha Provides Updates for all their Clinical Trials (CAN, US, UK)
January 16, 2024
A Concise Summary of Gene Therapy Clinical Trials for Rett Syndrome
January 10, 2024
First Pediatric Patient Dosed in Taysha US Clinical Trial
December 27, 2023
Taysha Pediatric Gene Therapy Trial Is Open for Enrollment in US
November 29, 2023
Taysha Expands Age Eligibility for Canadian Clinical Trial
July 31, 2023
Taysha Cleared to Dose Second Patient in Gene Therapy Trial
June 5, 2023
Taysha Gene Therapies Doses First Rett Syndrome Patient
February 1, 2023
Taysha Provides Update For Their Rett Syndrome Gene Replacement Program
January 10, 2023
The Story Behind Mini-MeCP2
December 19, 2022
What We Accomplished in 2022
1
2
$
40M
Take Action