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Cures
Roadmap to Cures
Where We’ve Been
Roadmap 1.0
Delivery
Viral
Non-Viral
Small RNA
Cargo
Gene Therapy
Base Editing
Prime Editing
MECP2 Reactivation
RNA Editing
RNA Trans-splicing
Tracking
Rett Syndrome Global Registry
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Biomarkers
Biosensors
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Families
Recently Diagnosed
For All Families
About Rett Syndrome
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Get Started Now
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NIH
April 18, 2025
How Will Cuts to FDA and NIH Impact Gene Therapy Clinical Trials and Rett Syndrome Research?
March 27, 2021
Taysha Gene Therapies Statement on Covid-19 Vaccines
November 19, 2018
New Method Developed to Study MeCP2 Function in Humans
April 25, 2017
Racing Down The Gene Therapy Highway To A Cure
May 20, 2014
Transparency in Clinical Trials
April 29, 2014
Chasing Cures: Reinventing the Business of Medicine
November 11, 2013
One Person Many Genomes
December 11, 2012
Who’s In Charge?
December 6, 2012
NIH Funding Woes
May 15, 2012
Treating Synaptic Dysfunction
$
40M
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