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Neurogene

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November 6, 2025
Neurogene Doses First Participant in Embolden™ Registrational Trial of NGN-401 for Rett Syndrome
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June 30, 2025
Neurogene Announces Trial Design for Embolden™ Study of NGN-401 Gene Therapy for Rett Syndrome
Ben Deverman, PhD | Senior Director of Vector Engineering at the Broad Institute of MIT and Harvard
April 18, 2025
How Will Cuts to FDA and NIH Impact Gene Therapy Clinical Trials and Rett Syndrome Research?
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January 15, 2025
A Review of Gene Therapy Clinical Trials
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November 30, 2024
Staying Resolute in Challenging Times
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November 21, 2024
With Heavy Hearts
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November 18, 2024
Neurogene Releases Update on NGN-401 Clinical Trial High Dose
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November 11, 2024
Neurogene Announces Interim Results from Gene Therapy Clinical Trial
FDA Selects Neurogene Rett Program for START Pilot Program
June 3, 2024
FDA Selects Neurogene Rett Program for START Pilot Program
Neurogene Announces Updates to Pediatric Gene Therapy Clinical Trial
March 4, 2024
Neurogene Announces Updates to Pediatric Gene Therapy Clinical Trial
Gene Therapy for Rett Highlights 2023
January 16, 2024
A Concise Summary of Gene Therapy Clinical Trials for Rett Syndrome
Neurogene doses first two children in gene therapy trial
November 30, 2023
Neurogene Doses First Two Patients in Pediatric US Trial
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June 12, 2023
Details on Neurogene Gene Therapy Trial Now on ClinicalTrial.gov
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April 18, 2023
Neurogene Shares Key Information on Gene Therapy Clinical Trial with the Rett Community
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January 23, 2023
Neurogene Receives FDA Approval for Gene Replacement Clinical Trial for Rett Syndrome
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December 19, 2022
What We Accomplished in 2022
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November 29, 2022
Leading the Cure for Rett: In Gene Replacement, There’s No Replacement for RSRT
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July 1, 2022
A Conversation with Neurogene's Leadership
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