Skip to main content
Search
Cures
Roadmap to Cures
Where We’ve Been
Roadmap 1.0
Delivery
Viral
Non-Viral
Small RNA
Cargo
Gene Therapy
Base Editing
Prime Editing
MECP2 Reactivation
RNA Editing
RNA Trans-splicing
Tracking
Rett Syndrome Global Registry
Citizen Health
Biomarkers
Biosensors
VIBRANT
Families
Was your child
recently diagnosed?
We’re here for you.
Reach Out Now
Recently Diagnosed
For All Families
About Rett Syndrome
Genetics Primer
Rett Syndrome Global Registry
Rett Clinics & Clinical Trials
Thriving with Rett Guides
Rett Fact Cards
Researchers
Fundraise
Start Your Own
Crowdfunding Page
We’ll get you set up!
Get Started
Get Started Now
Join Us
Events
RettGive Campaigns
Facebook Fundraisers
Donate
About Us
News
Get timely, factual news about Rett syndrome.
Browse News
Articles
Research
Community
Fundraising
Press Releases
Rett in the News
Donate
Join Us
Donate
Join Us
Cures
Roadmap to Cures
Where We’ve Been
Roadmap 1.0
Delivery
Viral
Non-Viral
Small RNA
Cargo
Gene Therapy
Base Editing
Prime Editing
MECP2 Reactivation
RNA Editing
RNA Trans-splicing
Tracking
Rett Syndrome Global Registry
Citizen Health
Biomarkers
Biosensors
VIBRANT
Families
Recently Diagnosed
For All Families
About Rett Syndrome
Genetics Primer
Rett Syndrome Global Registry
Rett Clinics & Clinical Trials
Thriving with Rett Guides
Rett Fact Cards
Researchers
Fundraise
Get Started Now
Join Us
Events
RettGive Campaigns
Facebook Fundraisers
Donate
About Us
News
Articles
Research
Community
Fundraising
Press Releases
Rett in the News
Rett Syndrome Global Registry
RettGive
Search
Alcyone
November 29, 2022
Leading the Cure for Rett: In Gene Replacement, There’s No Replacement for RSRT
November 10, 2022
What do astronauts and people living with Rett have in common?
December 7, 2021
How RSRT is driving the search for a Rett cure
May 26, 2021
Seven New RSRT-Supported Therapeutics Make Their Way Towards Clinical Trials
May 12, 2021
Introducing ACTX 101, a Gene Therapy for Rett Using X Reactivation Technology
$
40M
Take Action