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Articles
May 19, 2023
"There are no 'crazy experiments' when it comes to Rett"
April 18, 2023
Neurogene Shares Key Information on Gene Therapy Clinical Trial with the Rett Community
April 12, 2023
An Update on the New Rett Digital Natural History Study: How Our Children’s Medical Records Created a Decades-Long Study in Months
March 23, 2023
DAYBUE (trofinetide): Key Facts for Parents
March 20, 2023
Fundraising in Small Town, USA
March 13, 2023
Cures for Many Rare Disorders Will Come More Quickly Because of Digital Natural History Studies
March 7, 2023
Using Cerebral Organoids to Develop MECP2-Activating Drugs for Rett Syndrome
March 6, 2023
Remembering Michael R. Green (1954-2023): An eminent biologist who broke the monotony of mammalian transcription
March 3, 2023
What Wearables and AI Can Tell Us About Rett Syndrome Severity
February 9, 2023
New Study Demonstrates MECP2 Reactivation
February 1, 2023
Taysha Provides Update For Their Rett Syndrome Gene Replacement Program
January 23, 2023
Neurogene Receives FDA Approval for Gene Replacement Clinical Trial for Rett Syndrome
January 10, 2023
The Story Behind Mini-MeCP2
December 19, 2022
What We Accomplished in 2022
December 13, 2022
What We Learned from Taysha’s Clinical Trial Community Update
December 12, 2022
How You Can Take Action for Rett Research: The Only Wrong Way To Do It Is To Not Do It
December 7, 2022
Why Biosensors Will Revolutionize How Treatments Are Evaluated
December 5, 2022
The Most Important Research Factor: You
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