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Cures
Roadmap to Cures
Where We’ve Been
Roadmap 1.0
Delivery
Viral
Non-Viral
Small RNA
Cargo
Gene Therapy
Base Editing
Prime Editing
MECP2 Reactivation
RNA Editing
RNA Trans-splicing
Tracking
Rett Syndrome Global Registry
Citizen Health
Biomarkers
Biosensors
VIBRANT
Families
Recently Diagnosed
For All Families
About Rett Syndrome
Genetics Primer
Rett Syndrome Global Registry
Rett Clinics & Clinical Trials
Thriving with Rett Guides
Rett Fact Cards
Researchers
Fundraise
Get Started Now
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RettGive Campaigns
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Clinical Initiatives
June 20, 2016
First Impressions
March 8, 2016
$9 Million Awarded to Research
January 12, 2016
It’s All About the Sneakers
September 10, 2014
Guest Blogger: Drug Therapies and Rett
October 26, 2012
Innovation Meets Experience
March 28, 2012
Bone Marrow Transplants – Proceeding with Caution
March 18, 2012
Bone Marrow Transplant Stops the Development of Symptoms in Model of Rett Syndrome
July 7, 2010
Yet Another Door Opens: Neuroimmunology
1
2
$
40M
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