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Cures
Roadmap to Cures
Where We’ve Been
Roadmap 1.0
Delivery
Viral
Non-Viral
Small RNA
Cargo
Gene Therapy
Base Editing
Prime Editing
MECP2 Reactivation
RNA Editing
RNA Trans-splicing
Tracking
Rett Syndrome Global Registry
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Biomarkers
Biosensors
VIBRANT
Families
Recently Diagnosed
For All Families
About Rett Syndrome
Genetics Primer
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Get Started Now
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Children’s Hospital at Montefiore
November 24, 2015
Einstein Magazine Feature on Rett Syndrome
September 25, 2015
Seven Years and Counting
February 6, 2015
RSRT Awards $5.8 Million For Research and Two Clinical Trials
August 12, 2013
2013 Scientific Investments To Date
March 28, 2012
Bone Marrow Transplants – Proceeding with Caution
May 26, 2010
Curing Rett Syndrome: How do we get there? PART II
March 17, 2010
Scoliosis in Rett Syndrome
July 27, 2009
Curing Rett Syndrome: How Do We Get There?
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