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Cures
Roadmap to Cures
Where We’ve Been
Roadmap 1.0
Delivery
Viral
Non-Viral
Small RNA
Cargo
Gene Therapy
Base Editing
Prime Editing
MECP2 Reactivation
RNA Editing
RNA Trans-splicing
Tracking
Rett Syndrome Global Registry
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Recently Diagnosed
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Baylor College of Medicine
October 15, 2015
Deep Brain Stimulation – A Potential Therapeutic for Rett Syndrome?
February 6, 2015
RSRT Awards $5.8 Million For Research and Two Clinical Trials
February 26, 2014
On the Hunt for Modifiers
July 28, 2013
RSRT-funded Study Shows Cholesterol-Lowering Drugs Suppress Rett Symptoms
March 6, 2013
Boys With Rett Give Us Clues About MeCP2’s Function
November 19, 2012
Four Challenges in Rett Translational Research
September 29, 2009
The Upside of Genetic Mutations
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40M
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