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Cures
Roadmap to Cures
Where We’ve Been
Roadmap 1.0
Delivery
Viral
Non-Viral
Small RNA
Cargo
Gene Therapy
Base Editing
Prime Editing
MECP2 Reactivation
RNA Editing
RNA Trans-splicing
Tracking
Rett Syndrome Global Registry
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Biomarkers
Biosensors
VIBRANT
Families
Recently Diagnosed
For All Families
About Rett Syndrome
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Get Started Now
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Angelman syndrome
September 23, 2021
Taysha Gene Therapies Announces Age Range For First Trial During Educational Rett Event for Investors
July 29, 2021
A Reason to Celebrate: Children with a Severe Neurological Disorder Improve After Gene Replacement
February 9, 2013
Funding Research - Funding Results: Record $4.2 Million Awarded
May 15, 2012
Treating Synaptic Dysfunction
December 22, 2011
The X Factor
June 2, 2011
Rett Syndrome: Neurodevelopmental No Longer
$
40M
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