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Rett In The News

Fierce Biotech
June 9, 2021
The Massachusetts biotech unveiled itself Wednesday with $23 million in funding from RTW Investments with a pipeline of 12 adeno-associated virus (AAV) gene therapy programs for severe CNS disorders. Alcyone lead programs include ACTX-101, a Rett syndrome gene therapy in pre-IND enabling ...
St. Thomas Source
June 9, 2021
Ella Gaspard, a Virgin Islander, is diagnosed with Rett Syndrome. Ella’s Hope invites the public to join it on the first STT Cross-Island Challenge Ride to be held on July 3. One hundred percent of all proceeds raised from the STT Cross-Island Challenge will be donated to Rett Syndrome ...
Endpoints News
May 28, 2021
“This is the way to do it, to discover drugs for neurological diseases,” says Sharath Hegde “And it’s not going to be easy, but this is the way to do it.” And the company's lead program is Rett Syndrome.
May 27, 2021
Herophilus appoints a new Chief Scientific Officer and sets its sight on Rett Syndrome.
Endpoints News
May 25, 2021
RNA used to be considered a bit player. DNA was the start. Today it's a different story....
Shoutout LA
May 10, 2021
I’m proud of the work we have done at my production company, Peak Curiosity, and with the charitable advocacy work we do at Magnolia’s Hope on behalf of my daughter who suffers from Rett Syndrome.
Taysha Gene Therapies
May 10, 2021
Taysha Gene Therapies announces the publication of new preclinical data for their Rett Syndrome program, TSHA-102.
April 26, 2021
Farmingdale pharmaceutical firm DepYmed is no stranger to capital investments – but a new infusion might be enough to push the rare-disease innovator over the commercialization line.
Behavioral Training Could Help Babies with Rett Syndrome, Mouse Study Suggests
March 24, 2021
In mouse models of Rett Syndrome intensive training in young mice staved off symptoms of the disorder suggesting that perhaps the same might be true in people.
University of Connecticut
March 23, 2021
UConn professor of physiology and neurobiology Daniel Mulkey has received a $2.1 million grant from the NIH to investigate the cellular and molecular basis for disordered breathing in Rett syndrome. This project is part of a collaboration with Michelle Olsen, associate professor of neurobiology ...
UVA Health
March 15, 2021
UVA’s Sanchita Bhatnagar, PhD, discovered that tiny bits of RNA, called microRNAs, play an important role in Rett, a rare genetic disorder that can impair children’s ability to speak, move and even breathe.
Texas Children's Hospital
ASO as a feasible therapy to treat MECP2 duplication disorder
March 4, 2021
A study by Dr. Zoghbi provides experimental evidence that supports the use of antisense oligonucleotides as a feasible strategy to treat MECP2 Duplication Syndrome. Funding for this work came from the MECP2 Duplication Syndrome Fund at RSRT.
Rett Syndrome Awareness on Anderson Coooper's Full Circle
March 2, 2021
Four girls with Rett Syndrome and their moms discuss what they are grateful for in the "For Goods" section of "Full Circle"
March 1, 2021
Altering a protein linked to Rett syndrome so that it cannot bind to a particular type of DNA tag may explain the syndrome’s delayed onset in people.
Taysha Gene Therapies
February 17, 2021
Taysha Gene Therapies provides an update to the Rett Syndrome community on their Rett program, TSHA-102.
The Washington Post
February 13, 2021
The long wait for vaccination has left many people across the country feeling anxious, desperate even. But for the young and disabled, and for the people who care about them, the realization of where they fall on priority lists has also left them feeling disregarded and discarded.